RG7800

≥99%

  • Product Code: 102308
  CAS:    1449598-06-4
Molecular Weight: 416.52 g./mol Molecular Formula: C₂₄H₂₈N₆O
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Density: Storage Condition: 2-8℃
Product Description: RG7800 is primarily investigated for its potential therapeutic applications in treating neurodegenerative diseases, particularly spinal muscular atrophy (SMA). It functions as a small molecule modulator of the splicing of the SMN2 gene, which is crucial for increasing the production of survival motor neuron (SMN) protein. This mechanism is vital because SMA is characterized by a deficiency in SMN protein, leading to motor neuron degeneration and muscle weakness. By enhancing SMN protein levels, RG7800 aims to improve motor function and slow disease progression in SMA patients. Its development represents a promising approach in the field of genetic medicine, offering hope for effective treatment options for this debilitating condition.
Sizes / Availability / Pricing:
Size (g) Availability Price Quantity
0.005 10-20 days $578.22
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0.010 10-20 days $915.52
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RG7800
RG7800 is primarily investigated for its potential therapeutic applications in treating neurodegenerative diseases, particularly spinal muscular atrophy (SMA). It functions as a small molecule modulator of the splicing of the SMN2 gene, which is crucial for increasing the production of survival motor neuron (SMN) protein. This mechanism is vital because SMA is characterized by a deficiency in SMN protein, leading to motor neuron degeneration and muscle weakness. By enhancing SMN protein levels, RG7800 aims to improve motor function and slow disease progression in SMA patients. Its development represents a promising approach in the field of genetic medicine, offering hope for effective treatment options for this debilitating condition.
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