Veledimex is primarily used in the field of gene therapy and immunotherapy. It functions as a small molecule activator, specifically designed to regulate gene expression in engineered T-cell therapies. One of its key applications is in the treatment of certain cancers, where it is used to enhance the activity of chimeric antigen receptor (CAR) T-cells. By controlling the expression of therapeutic genes, Veledimex helps improve the precision and effectiveness of these treatments while minimizing off-target effects. Additionally, it plays a role in research studies focused on understanding and optimizing gene regulation systems in advanced medical therapies.