SMN-C3 is primarily utilized in the field of medicinal chemistry, particularly in the development of treatments for spinal muscular atrophy (SMA). It functions as a small molecule modulator that enhances the production of survival motor neuron (SMN) protein, which is crucial for motor neuron health. This compound is being explored for its potential to improve motor function and overall survival in patients with SMA, offering a promising therapeutic approach. Additionally, SMN-C3 is studied for its role in combination therapies, aiming to maximize efficacy and provide more comprehensive treatment options for this genetic disorder.