Veledimex racemate is primarily used in the field of gene therapy and immunotherapy. It serves as an activator for gene switches in engineered immune cells, particularly in chimeric antigen receptor (CAR) T-cell therapies. By crossing the blood-brain barrier, it enables precise control over gene expression in targeted cells, enhancing the effectiveness of treatments for cancers, including brain tumors. Its application is also explored in regulating therapeutic genes in other conditions, offering a versatile tool for advanced medical interventions.